Gene therapy was first attempted to treat a patient with which genetic disorder? MCQ with Answer and Explanation

Gene therapy was first attempted to treat a patient with which genetic disorder?
A. Hemophilia
B. Sickle cell anemia
C. Cystic fibrosis
D. Adenosine Deaminase (ADA) deficiency
Answer: Option D
Solution (By JKExamLibrary)
Gene therapy involves correcting a genetic defect by introducing a functional gene into a patient's cells. The first clinical gene therapy was given in 1990 to a 4-year-old girl with Adenosine Deaminase (ADA) deficiency, a severe combined immunodeficiency (SCID) caused by a mutation in the ADA gene. The functional ADA gene was introduced into her lymphocytes using a retroviral vector.

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